gene therapy Archives - Express Pharma

FDA expands approval of gene therapy for patients with Duchenne Muscular Dystrophy

Beacon Therapeutics’ AGTC-501 holds potential to become first gene therapy in XLRP space: GlobalData

CRISPR-based innovations drive $21 bn in pharma licensing deals over five years: GlobalData

US approves first gene therapy for children with rare genetic disease

EMA seeks to issue guidance on liver damage from Novartis’s gene therapy

US FDA approves Bluebird Bio’s gene therapy for rare neurological disorder

Pfizer to start US trial of gene therapy as FDA lifts hold

Novartis and Voyager Therapeutics reach licence option agreement for next-generation gene therapy vectors for neurological diseases

CPhI and Informa Pharma Intelligence conclude 3rd Biopharma Conclave

TSHA-102 from Taysha gets rare paediatric disease and orphan drug designations for Rett syndrome